Vice President, Medical Affairs Rare Diseases

Overview

In this role you will provide strategic medical leadership across the Rare Diseases portfolio, guiding medical affairs and evidence generation to support growth. You will partner with clinical development, regulatory, and commercial teams to shape global medical strategies while upholding ethics and patient centricity. As a scientific external spokesperson, you will strengthen relationships with KOLs and societies to advance patient-centered advocacy. This is a fast-paced, collaborative leadership role focused on robust medical governance and cross-functional impact.

Responsabilità

• Develop and implement integrated Medical Affairs strategies for rare diseases products
• Lead creation of Integrated Evidence Plans aligned with development, regulatory, market access, and commercial teams
• Provide medical leadership across the BU and guide lifecycle management for rare disease assets
• Contribute medical input to BD assessments and post-marketing studies
• Collaborate with Medical Evidence Generation Lead to design global evidence generation (including RWE, ISS)
• Build and mentor a high-performing Medical Affairs community; ensure training and alignment across global and affiliate levels
• Support early development and launch readiness for new indications and assets
• Maintain proactive medical input to Clinical Development, Regulatory Affairs, Market Access, Pharmacovigilance, and Commercial teams
• Engage with KOLs, scientific societies, healthcare professionals, and patient groups; develop medical education programs for rare disease stakeholders
• Represent the company's medical perspective externally in partnership with Patient Partnership teams; advance patient-centered advocacy
• Define and monitor KPIs for Medical Affairs initiatives and manage the Medical Affairs budget
• Ensure compliance with SOPs, ethics, and regulatory requirements; collaborate on governance for rare disease products and compassionate use programs

Requisiti fondamentali

• 20+ years in the pharmaceutical industry with global or regional Medical Affairs leadership
• MD degree required
• Board certification in a relevant specialty preferred
• Proven ability to define and execute medical strategies that enhance product value and lifecycle in rare diseases
• Strong scientific and analytical capabilities to translate data into strategic insights
• Credibility with KOLs, scientific societies, regulatory bodies, and external partners
• Deep understanding of global medical governance, compliance, pharmacovigilance, and regulatory frameworks
• Track record of building high-performing medical teams and fostering scientific excellence and ethical decision-making
• Experience in multicultural, matrixed environments with cross-functional alignment
• leadership with clear direction
• cross-functional collaboration
• excellent communication
• Medical strategy and leadership
• Evidence generation (RWE, ISS)
• Regulatory and pharmacovigilance knowledge